ABSTRACT

Rare Diseases: Expediting Treatments for Patients, Hearing Before the Subcommittee on Children and Families of the Committee on Health, Education, Labor, and Pensions, United States Senate, One Hundred Fifteenth Congress, Second Session, October 3, 2018   [open pdf - 302KB]

This is the October 3, 2018 hearing on "Rare Diseases: Expediting Treatments for Patients," held before the U.S. Senate Subcommittee on Children and Families of the Committee on Health, Education, Labor, and Pensions,. From the opening statement of Rand Paul: "We are here today to talk about a critically important issue: the development of drugs to treat rare diseases. Thirty-five years ago, Congress passed the landmark Orphan Drug Act. This legislation represented the first concerted Federal effort to incentivize the development of new treatments specifically for rare diseases. The Orphan Drug Act established grants to assist in the development of new orphan drugs." Statements, letters, and materials submitted for the record include those of the following: Mark Dant, Marc Patterson, Michael Strupp, Lincoln Tsang, and Mallory Factor.

Report Number:
S. Hrg. 115-851; Senate Hearing. 115-851
Publisher:
Date:
2020
Copyright:
Public Domain
Retrieved From:
U.S. Government Publishing Office: http://www.gpo.gov/
Format:
pdf
Media Type:
application/pdf
URL:
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